MRNA-Based Therapeutics

MRNA-Based Therapeutics

Galluzzi, Lorenzo; Aranda Vega, Fernando; Berraondo, Pedro

Elsevier Science & Technology

09/2022

326

Dura

Inglês

9780323994019

15 a 20 dias

450

Descrição não disponível.
1. New era of nucleic acid therapies: Clinical applications and perspectives Andoni Garitano 2. Messenger RNA as personalized therapy: time of truth for rare metabolic disease Antonio fontanellas 3. Applications of Self-Replicating RNA Kenneth Lundstrom 4. mRNA therapy in PKU Ramon Diaz Trelles 5. Advances in gene-editing technologies Robert MacLaren and Ruofan Connie Han 6. mRNA delivery technologies: towards clinical translation Maria Angeles Solinis 7. Advances in mRNA vaccines Xiaojun Xia
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RNA editing; CRISPR; ADAR; CIRTS; LEAPER; BoxB; GluR2; SNAP; Cas13; gene editing; gene therapy; retina